In a move that continues a recent bolstering of its gene therapy pipeline, Eli Lilly has signed a global research ...

Gene-editing tools like CRISPR have unlocked new treatments for previously uncurable diseases. Now, researchers at the ...

The development of a brain tumor in a study participant led regulators to suspend a Hurler syndrome therapy in early testing ...

A central nervous system (CNS) tumor has prompted the FDA to place clinical holds on two Regenxbio gene therapies, including ...

The company said that the FDA hold has impacted two experimental gene therapies, RGX-111 and RGX-121. ・REGENXBIO added that ...

While the clinical hold has been lifted on the MAGNITUDE-2 trial, it remains in place on the MAGNITUDE study.

Intellia Therapeutics said on Tuesday that the U.S. drug regulator has lifted a clinical hold on one of its late-stage gene ...

(Yicai) Jan. 28 -- Chinese medical researchers have made a breakthrough in gene therapy that overcomes the limitations of ...

A new CRISPR-based one-off procedure that lowers "bad" cholesterol has been approved to enter Phase I human trial. If ...

OCU410 controlled lesion growth 46% better than placebo in dAMD-related GA.

University of California San Diego-led team has discovered that restoring a key cardiac protein called connexin‑43 in a mouse ...

Opus Genetics is conducting a trial for OPGx-MERTK gene therapy in Abu Dhabi, targeting MERTK-related retinitis pigmentosa ...