Researchers led by the University of Vienna and Liège University Hospital Center have identified genetic variants associated ...
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DiMe introduces core digital measures set to accelerate drug development for pediatric rare diseases
The Digital Health Measurement Collaborative Community (DATAcc) by the Digital Medicine Society (DiMe) today announced the ...
Brelovitug has received breakthrough therapy designation from the US Food and Drug Administration.
Rare disease clinical trials are smaller and often use surrogate endpoints, reducing costs but posing unique operational ...
Some 200 rare disease therapies are at risk of losing eligibility for a pediatric priority review voucher, a recent analysis ...
Researchers at UCL and Great Ormond Street Hospital (GOSH) have developed the first-ever lab-grown mini-stomach that contains ...
Ashleigh McGeogh's daughter Delilah was diagnosed with Kawasaki disease, a condition that is the leading cause of acquired ...
Jaguar has received the initial $16M payment related to the company's recently executed US out-license agreement for ...
In its new incarnation, apecotrep has been shown to reduce protein in the urine (proteinuria) – a biomarker for kidney ...
Dr Sudheendra Rao N R from the Organization for Rare Diseases India reveals that approximately 70 million are affected by ...
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